Evidence mapPaperPMID 32948541Full record

SynthesisBMJ open2020

Crizanlizumab and comparators for adults with sickle cell disease: a systematic review and network meta-analysis.

Howard Thom, Jeroen Jansen, Jason Shafrin, Lauren Zhao, George Joseph, Hung-Yuan Cheng, Subhajit Gupta, Nirmish Shah

Open access · goldAbstract readNetwork Meta-AnalysisSystematic Review
In one paragraph

Synthesis in BMJ open, 2020. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 5 papers.

0numbers the graph read from it
0cells of the map it votes in
5citing papers in PubMed
1.2field-weighted citation impact, top 22% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

5 citing papers in PubMed, 11 citations in OpenAlex.

  1. Article
  2. Article
  3. Article
  4. Article
  5. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors at 3 institutions in 2 countries.

Howard ThomBristol Medical School, University of Bristol, Bristol, UK howard.thom@bristol.ac.uk.
Jeroen JansenHealth Economics, PRECISIONheor, Los Angeles, California, USA.
Jason ShafrinHealth Economics, PRECISIONheor, Los Angeles, California, USA.
Lauren ZhaoHealth Economics, PRECISIONheor, Los Angeles, California, USA.ORCID 0000-0001-6339-149X
George JosephNovartis Pharmaceuticals Corp, East Hanover, New Jersey, USA.
Hung-Yuan ChengBristol Medical School, University of Bristol, Bristol, UK.
Subhajit GuptaNovartis Pharmaceuticals Corp, East Hanover, New Jersey, USA.
Nirmish ShahDepartment of Medicine, Duke University, Durham, North Carolina, USA.
Novartis (United States) · USUniversity of Bristol · GBDuke University · US

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

objectivesTreatment options for preventing vaso-occlusive crises (VOC) among patients with sickle cell disease (SCD) are limited, especially if hydroxyurea treatment has failed or is contraindicated. A systematic literature review (SLR) and network meta-analysis (NMA) were conducted to evaluate the efficacy and safety of crizanlizumab for older adolescent and adult (≥16 years old) SCD patients.

methodsThe SLR included randomised controlled trials (RCTs) and uncontrolled studies. Bayesian NMA of VOC, all-cause hospitalisation days and adverse events were conducted.

resultsThe SLR identified 51 studies and 9 RCTs on 14 treatments that met the NMA inclusion criteria. The NMA found that crizanlizumab 5.0 mg/kg was associated with a reduction in VOC (HR 0.55, 95% credible interval (0.43, 0.69); Bayesian probability of superiority >0.99), all-cause hospitalisation days (0.58 (0.50, 0.68); >0.99) and no evidence of difference on adverse events (0.91 (0.59, 1.43) 0.66) or serious adverse events (0.93 (0.47, 1.87); 0.59) compared with placebo. The HR for reduction in VOC for crizanlizumab relative to L-glutamine was (0.67 (0.50, 0.88); >0.99). These results were sensitive to assumptions regarding whether patient age is an effect modifier.

conclusionsThis NMA provides preliminary evidence comparing the efficacy of crizanlizumab with other treatments for VOC prevention.

Indexed as

Anemia, Sickle CellAdultAntibodies, Monoclonal, HumanizedBayes TheoremHumansAntibodies, Monoclonal, Humanizedcrizanlizumabcrizanlizumabhematologynetwork meta-analysissickle cell diseasesystematic literature reviewvasoocclusive crisis

Identifiers

PMID32948541
PMCPMC7500297
OpenAlexW3042348937

What Socratic holds

Textmetadata
LicenceCC BY-NC
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Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.