Evidence mapPaperPMID 34000049Full record

Trial reportThe Journal of clinical endocrinology and metabolism2021

Randomized Controlled Trial of Neurokinin 3 Receptor Antagonist Fezolinetant for Treatment of Polycystic Ovary Syndrome.

Graeme L Fraser, Barbara Obermayer-Pietsch, Joop Laven, Georg Griesinger, Axelle Pintiaux, Dirk Timmerman, Bart C J M Fauser, Christopher Lademacher, Jean Combalbert, Hamid R Hoveyda and 1 more

Open access · bronzeAbstract readMulticenter StudyRandomized Controlled Trial
In one paragraph

Trial report in The Journal of clinical endocrinology and metabolism, 2021. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 23 papers, 1 of them a synthesis that pooled it.

0numbers the graph read from it
0cells of the map it votes in
23citing papers in PubMed, 1 pooled it
7.5field-weighted citation impact, top 2% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

23 citing papers in PubMed, 1 synthesis or guideline pooled it, 50 citations in OpenAlex.

  1. Pooled it
  2. Article
  3. Genetics of Idiopathic Hypogonadotropic HypogonadismJournal of clinical research in pediatric endocrinology · 2026
    Review
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  12. Review
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  19. Review
  20. Targeting KNDy neurons to control GnRH pulses.Current opinion in pharmacology · 2022
    Review
4 · The record

Corrections and comments

5 · Who and what money

Authors and funding

11 authors at 7 institutions in 5 countries.

Barbara Obermayer-PietschMedical University, 8036 Graz,Austria.
Joop LavenErasmus MC, 3015 Rotterdam, the Netherlands.
Georg GriesingerSchleswig-Holstein University Hospital, 23562 Lübeck,Germany.ORCID 0000-0002-0606-5804
Axelle PintiauxCHR Liège Citadelle Hospital, 4020 Liège,Belgium.
Dirk TimmermanUniversity Hospital, KU Leuven, 3000 Leuven, Belgium.
Bart C J M FauserUniversity Medical Center, 3584 Utrecht, the Netherlands.ORCID 0000-0002-3865-4371
Christopher LademacherAstellas Pharma US Inc, Northbrook, IL 60062,USA.
Jean Combalbert
Hamid R Hoveyda
Steven Ramael
Astellas Pharma (United States) · USCentre hospitalier régional de la Citadelle · BEErasmus MC · NLKU Leuven · BEMedical University of Graz · ATUniversity Hospital Schleswig-Holstein · DEUniversity Medical Center Utrecht · NL

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

contextPolycystic ovary syndrome (PCOS), a highly prevalent endocrine disorder characterized by hyperandrogenism, is the leading cause of anovulatory infertility.

objectiveThis proof-of-concept study evaluated clinical efficacy and safety of the neurokinin 3 (NK3) receptor antagonist fezolinetant in PCOS.

methodsThis was a phase 2a, randomized, double-blind, placebo-controlled, multicenter study (EudraCT 2014-004409-34). The study was conducted at 5 European clinical centers. Women with PCOS participated in the study. Interventions included fezolinetant 60 or 180 mg/day or placebo for 12 weeks. The primary efficacy end point was change in total testosterone. Gonadotropins, ovarian hormones, safety and tolerability were also assessed.

resultsSeventy-three women were randomly assigned, and 64 participants completed the study. Adjusted mean (SE) changes in total testosterone from baseline to week 12 for fezolinetant 180 and 60 mg/day were -0.80 (0.13) and -0.39 (0.12) nmol/L vs -0.05 (0.10) nmol/L with placebo (P < .001 and P < .05, respectively). Adjusted mean (SE) changes from baseline in luteinizing hormone (LH) for fezolinetant 180 and 60 mg/d were -10.17 (1.28) and -8.21 (1.18) vs -3.16 (1.04) IU/L with placebo (P < .001 and P = .002); corresponding changes in follicle-stimulating hormone (FSH) were -1.46 (0.32) and -0.92 (0.30) vs -0.57 (0.26) IU/L (P = .03 and P = .38), underpinning a dose-dependent decrease in the LH-to-FSH ratio vs placebo (P < .001). Circulating levels of progesterone and estradiol did not change significantly vs placebo (P > .10). Fezolinetant was well tolerated.

conclusionFezolinetant had a sustained effect to suppress hyperandrogenism and reduce the LH-to-FSH ratio in women with PCOS.

Indexed as

AdolescentAdultDose-Response Relationship, DrugDouble-Blind MethodFemaleFollicle Stimulating HormoneGonadotropinsHeterocyclic Compounds, 2-RingHumansHyperandrogenismLuteinizing HormoneMiddle AgedOvarian Function TestsPolycystic Ovary SyndromeReceptors, Neurokinin-3TestosteronefezolinetantFollicle Stimulating HormoneGonadotropinsHeterocyclic Compounds, 2-RingLuteinizing HormoneReceptors, Neurokinin-3TestosteroneThiadiazolesdynorphin A neuronsgonadotropin-releasing hormonekisspeptinneurokinin 3 receptorneurokinin Bpolycystic ovary syndrome

Identifiers

PMID34000049
PMCPMC8372662
OpenAlexW3162519732

What Socratic holds

Textmetadata
LicenceCC BY-NC-ND
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.