Evidence mapPaperPMID 34058071Full record

Trial reportClinical and translational science2021

Translational and pharmacokinetic-pharmacodynamic application for the clinical development of GDC-0334, a novel TRPA1 inhibitor.

Phyllis Chan, Han Ting Ding, Bianca M Liederer, Jialin Mao, Paula Belloni, Liuxi Chen, Simon S Gao, Victory Joseph, Xiaoying Yang, Joseph S Lin and 5 more

Open access · goldAbstract readClinical Trial, Phase IRandomized Controlled Trial
In one paragraph

Trial report in Clinical and translational science, 2021. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 8 papers.

0numbers the graph read from it
0cells of the map it votes in
8citing papers in PubMed
1.6field-weighted citation impact, top 20% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

8 citing papers in PubMed, 20 citations in OpenAlex.

  1. Trial
  2. Trial
  3. The role of TRPA1 in lung cancer.Translational lung cancer research · 2025
    Review
  4. Article
  5. Review
  6. Review
  7. Discovery ofJournal of medicinal chemistry · 2023
    Article
  8. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

15 authors at 1 institution in 1 country.

Phyllis ChanDepartment of Clinical Pharmacology, Genentech, Inc, South San Francisco, California, USA.ORCID 0000-0003-1509-1526
Han Ting DingDepartment of Clinical Pharmacology, Genentech, Inc, South San Francisco, California, USA.
Bianca M LiedererDepartment of Drug Metabolism & Pharmacokinetics, Genentech, Inc, South San Francisco, California, USA.
Jialin MaoDepartment of Drug Metabolism & Pharmacokinetics, Genentech, Inc, South San Francisco, California, USA.
Paula BelloniDepartment of Clinical Sciences, Early Clinical Development, Genentech, Inc, South San Francisco, California, USA.
Liuxi ChenDepartment of Drug Metabolism & Pharmacokinetics, Genentech, Inc, South San Francisco, California, USA.
Simon S GaoDepartment of Clinical Imaging, Genentech, Inc, South San Francisco, California, USA.
Victory JosephDepartment of Biomedical Imaging, Genentech, Inc, South San Francisco, California, USA.
Xiaoying YangDepartment of Biostatistics, Early Clinical Development, Genentech, Inc, South San Francisco, California, USA.
Joseph S LinDepartment of Clinical Sciences, Early Clinical Development, Genentech, Inc, South San Francisco, California, USA.
Mayur S MitraDepartment of Toxicology, Genentech, Inc, South San Francisco, California, USA.
Wendy S PutnamDepartment of Clinical Pharmacology, Genentech, Inc, South San Francisco, California, USA.
Angelica QuartinoDepartment of Clinical Pharmacology, Genentech, Inc, South San Francisco, California, USA.ORCID 0000-0003-0184-4670
Rebecca N BauerDepartment of Biomarker Development, Early Clinical Development, Genentech, Inc, South San Francisco, California, USA.
Lin PanDepartment of Clinical Pharmacology, Genentech, Inc, South San Francisco, California, USA.
Sunesis (United States) · US

Funding

Genentech/Roche
6 · The paper itself

Abstract

GDC-0334 is a novel small molecule inhibitor of transient receptor potential cation channel member A1 (TRPA1), a promising therapeutic target for many nervous system and respiratory diseases. The pharmacokinetic (PK) profile and pharmacodynamic (PD) effects of GDC-0334 were evaluated in this first-in-human (FIH) study. A starting single dose of 25 mg was selected based on integrated preclinical PK, PD, and toxicology data following oral administration of GDC-0334 in guinea pigs, rats, dogs, and monkeys. Human PK and PK-PD of GDC-0334 were characterized after single and multiple oral dosing using a population modeling approach. The ability of GDC-0334 to inhibit dermal blood flow (DBF) induced by topical administration of allyl isothiocyanate (AITC) was evaluated as a target-engagement biomarker. Quantitative models were developed iteratively to refine the parameter estimates of the dose-concentration-effect relationships through stepwise estimation and extrapolation. Human PK analyses revealed that bioavailability, absorption rate constant, and lag time increase when GDC-0334 was administered with food. The inhibitory effect of GDC-0334 on the AITC-induced DBF biomarker exhibited a clear sigmoid-Emax relationship with GDC-0334 plasma concentrations in humans. This study leveraged emerging preclinical and clinical data to enable iterative refinement of GDC-0334 mathematical models throughout the FIH study for dose selection in subsequent cohorts throughout the study. Study Highlights WHAT IS THE CURRENT KNOWLEDGE ON THE TOPIC? GDC-0334 is a novel, small molecule TRPA1 inhibitor and a pharmacokinetic-pharmacodynamic (PK-PD) modeling strategy could be implemented in a systematic and step-wise manner to build and learn from emerging data for early clinical development. WHAT QUESTION DID THIS STUDY ADDRESS? Can noncompartmental and population-based analyses be used to describe the PK and PD characteristics of GDC-0334 in preclinical and clinical studies? WHAT DOES THIS STUDY ADD TO OUR KNOWLEDGE? GDC-0334 exposure generally increased with dose in rats, dogs, and monkeys. The starting dose (25 mg) in the clinical study was determined based on the preclinical data. GDC-0334 exhibited linear PK in humans and the bioavailability was increased with food. The inhibitory effect of GDC-0334 on dermal blood flow induced by the TRPA1 agonist allyl isothiocyanate in humans indicates a clear PK-PD relationship. HOW MIGHT THIS CHANGE CLINICAL PHARMACOLOGY OR TRANSLATIONAL SCIENCE? The models developed based on TRPA1 agonist-induced dermal blood flow inhibition data can be used to predict PK-PD relationships in future preclinical and clinical studies evaluating new drug entities that target TRPA1.

Indexed as

Models, BiologicalAdministration, IntravenousAdultAnimalsBiological AvailabilityDogsDose-Response Relationship, DrugDrug Evaluation, PreclinicalFemaleGastrointestinal AbsorptionHealthy VolunteersHumansIsothiocyanatesMacaca fascicularisMaleMiddle Agedallyl isothiocyanateGDC-0334IsothiocyanatesPyridinesPyrimidinesTRPA1 Cation ChannelTRPA1 protein, human

Identifiers

PMID34058071
PMCPMC8504827
OpenAlexW3164311578

What Socratic holds

Textmetadata
LicenceCC BY-NC-ND
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.