Evidence mapPaperPMID 35316212Full record

ArticleThe Journal of clinical investigation2022

Aerobic exercise elicits clinical adaptations in myotonic dystrophy type 1 patients independently of pathophysiological changes.

Andrew I Mikhail, Peter L Nagy, Katherine Manta, Nicholas Rouse, Alexander Manta, Sean Y Ng, Michael F Nagy, Paul Smith, Jian-Qiang Lu, Joshua P Nederveen and 2 more

Registry-linked trialOpen access · goldAbstract read
In one paragraph

Article in The Journal of clinical investigation, 2022. The graph could read no effect estimate from its abstract, so it casts no vote on the map. It is linked to trial NCT04187482 (Functional and Cellular Benefits of Aerobic Exercise in Myotonic Dystrophy Type 1 Patients), which is not on this map. Cited by 28 papers, 2 of them syntheses that pooled it.

0numbers the graph read from it
0cells of the map it votes in
28citing papers in PubMed, 2 pooled it
4.0field-weighted citation impact, top 5% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

NCT04187482 nacompletednot on this map

Functional and Cellular Benefits of Aerobic Exercise in Myotonic Dystrophy Type 1 Patients

TypeinterventionalSponsorMcMaster UniversityRan2019 to 2021Enrolled13ConditionsMyotonic Dystrophy 1, Muscular DystrophiesArmsExercise training
3 · Its place in the literature

Who cites it

28 citing papers in PubMed, 2 syntheses or guidelines pooled it, 43 citations in OpenAlex.

  1. Pooled it
  2. Pooled it
  3. Review
  4. Myopathies in clinical care: a focus on treatable causes.Journal of neural transmission (Vienna, Austria : 1996) · 2026
    Review
  5. Aberrant Splicing ofCirculation. Genomic and precision medicine · 2026
    Article
  6. Article
  7. Article
  8. Article
  9. HSAInternational journal of molecular sciences · 2025
    Article
  10. Review
  11. Review
  12. Skeletal muscle disorders as risk factors for type 2 diabetes.Molecular and cellular endocrinology · 2025
    Review
  13. Article
  14. Article
  15. Myotonic Dystrophy type 2 unmasked by physical activity resumption following COVID-19 lockdown: case discussion and review of the literature.Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology · 2024
    Review
  16. Article
  17. Article
  18. Article
  19. Article
  20. Studying the Effect of MBNL1 and MBNL2 Loss in Skeletal Muscle Regeneration.International journal of molecular sciences · 2024
    Article
4 · The record

Corrections and comments

5 · Who and what money

Authors and funding

12 authors at 4 institutions in 2 countries.

Andrew I MikhailDepartment of Kinesiology, McMaster University, Hamilton, Ontario, Canada.
Peter L NagyPraxis Genomics LLC, Atlanta, Georgia, USA.
Katherine MantaDepartment of Pediatrics, McMaster University Children's Hospital, Hamilton, Ontario, Canada.
Nicholas RousePraxis Genomics LLC, Atlanta, Georgia, USA.
Alexander MantaDepartment of Kinesiology, McMaster University, Hamilton, Ontario, Canada.
Sean Y NgDepartment of Kinesiology, McMaster University, Hamilton, Ontario, Canada.
Michael F NagyPraxis Genomics LLC, Atlanta, Georgia, USA.
Paul SmithPraxis Genomics LLC, Atlanta, Georgia, USA.
Jian-Qiang LuDepartment of Pathology and Molecular Medicine/Neuropathology, McMaster University, Hamilton, Ontario, Canada.
Joshua P NederveenDepartment of Pediatrics, McMaster University Children's Hospital, Hamilton, Ontario, Canada.
Vladimir LjubicicDepartment of Kinesiology, McMaster University, Hamilton, Ontario, Canada.
Mark A TarnopolskyDepartment of Pediatrics, McMaster University Children's Hospital, Hamilton, Ontario, Canada.
McMaster University · CAPraxis (United States) · USMcMaster Children's Hospital · CAMcMaster University Medical Centre · CA

Funding

CIHR 143325
6 · The paper itself

Abstract

BackgroundMyotonic dystrophy type 1 (DM1) is a complex life-limiting neuromuscular disorder characterized by severe skeletal muscle atrophy, weakness, and cardiorespiratory defects. Exercised DM1 mice exhibit numerous physiological benefits that are underpinned by reduced CUG foci and improved alternative splicing. However, the efficacy of physical activity in patients is unknown.MethodsEleven genetically diagnosed DM1 patients were recruited to examine the extent to which 12 weeks of cycling can recuperate clinical and physiological metrics. Furthermore, we studied the underlying molecular mechanisms through which exercise elicits benefits in skeletal muscle of DM1 patients.RESULTSDM1 was associated with impaired muscle function, fitness, and lung capacity. Cycling evoked several clinical, physical, and metabolic advantages in DM1 patients. We highlight that exercise-induced molecular and cellular alterations in patients do not conform with previously published data in murine models and propose a significant role of mitochondrial function in DM1 pathology. Finally, we discovered a subset of small nucleolar RNAs (snoRNAs) that correlated to indicators of disease severity.ConclusionWith no available cures, our data support the efficacy of exercise as a primary intervention to partially mitigate the clinical progression of DM1. Additionally, we provide evidence for the involvement of snoRNAs and other noncoding RNAs in DM1 pathophysiology.Trial registrationThis trial was approved by the HiREB committee (no. 7901) and registered under ClinicalTrials.gov (NCT04187482).FundingNeil and Leanne Petroff. Canadian Institutes of Health Research Foundation (no. 143325).

Indexed as

Myotonic DystrophyPhysical Conditioning, AnimalAlternative SplicingAnimalsCanadaHumansMiceMuscle, SkeletalCell BiologyMitochondriaMuscle BiologyNeuromuscular diseaseRNA processing

Identifiers

PMID35316212
PMCPMC9106360
OpenAlexW4220752453

What Socratic holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.