Evidence map›Paper›PMID 36749302›Full record

Trial reportJournal of comparative effectiveness research2023

Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status.

Craig M McDonald, Jessica R Marden, Perry B Shieh, Brenda L Wong, Henry Lane, Adina Zhang, Ha Nguyen, Molly Frean, Panayiota Trifillis, Karyn Koladicz and 1 more

Registry-linked trialOpen access · diamondAbstract readClinical Trial, Phase IIClinical Trial, Phase III
PubMed Full text at PMC Publisher
In one paragraph

Trial report in Journal of comparative effectiveness research, 2023. The graph could read no effect estimate from its abstract, so it casts no vote on the map. It is linked to trial NCT06747884 (Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension), which is not on this map. Cited by 5 papers.

0numbers the graph read from it
0cells of the map it votes in
5citing papers in PubMed
1.8field-weighted citation impact, top 15% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

NCT06747884 recruitingnot on this mapstarted 2025, after this paper: background citation

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

TypeobservationalSponsorVirginia Commonwealth UniversityRan2025 to 2030Enrolled200ConditionsCongenital Myotonic Dystrophy, Childhood Myotonic Dystrophy, Myotonic Dystrophy
3 · Its place in the literature

Who cites it

5 citing papers in PubMed, 12 citations in OpenAlex.

  1. Trial
  2. Article
  3. Article
  4. Article
  5. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

11 authors at 5 institutions in 1 country.

Craig M McDonaldDepartments of Physical Medicine & Rehabilitation and Pediatrics, University of California - Davis, Davis, CA 95616, USA.ORCID 0000-0002-8779-3220
Jessica R MardenAnalysis Group, Inc., Boston, MA 02199, USA.ORCID 0000-0002-8360-7558
Perry B ShiehUCLA Health, Los Angeles, CA 90095, USA.
Brenda L WongDepartment of Pediatrics, University of Massachusetts Memorial Medical Center Worcester, MA 01605, USA.
Henry LaneAnalysis Group, Inc., Boston, MA 02199, USA.
Adina ZhangAnalysis Group, Inc., Boston, MA 02199, USA.
Ha NguyenAnalysis Group, Inc., Boston, MA 02199, USA.
Molly FreanAnalysis Group, Inc., Boston, MA 02199, USA.ORCID 0000-0002-5770-4266
Panayiota TrifillisPTC Therapeutics, Inc., South Plainfield, NJ 07080, USA.
Karyn KoladiczPTC Therapeutics, Inc., South Plainfield, NJ 07080, USA.
James SignorovitchAnalysis Group, Inc., Boston, MA 02199, USA.
Analysis Group (United States) · USPTC Therapeutics (United States) · USMemorial Medical Center · USUCLA Health · USUniversity of California, Davis · US

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

PubMed holds no abstract for this paper.

Indexed as

Muscular Dystrophy, DuchenneAdrenal Cortex HormonesChildDisease ProgressionFunctional StatusHumansPrednisoneAdrenal Cortex HormonesPrednisoneclinical outcomesdeflazacortdisease milestonesDuchenne muscular dystrophyefficacyprednisone/prednisolone

Identifiers

PMID36749302
PMCPMC10402754
OpenAlexW4319332816

What Socratic holds

Textmetadata
LicenceCC BY-NC-ND
Read underepoch 390

Registered trials

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.