Evidence map›Paper›PMID 37930769›Full record

ArticleThe Journal of clinical endocrinology and metabolism2024

Effect of Burosumab on Muscle Function and Strength, and Rates of ATP Synthesis in Skeletal Muscle in Adults With XLH.

Karl L Insogna, Rebecca Sullivan, Stephen Parziale, Yanhong Deng, Diana Carrano, Christine Simpson, Sylvie Dufour, Thomas Carpenter, Kitt Falk Petersen

Abstract read
In one paragraph

Article in The Journal of clinical endocrinology and metabolism, 2024. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 6 papers.

0numbers the graph read from it
0cells of the map it votes in
6citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

6 citing papers in PubMed.

  1. Article
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  5. Review
  6. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

9 authors.

Karl L InsognaDepartment of Medicine, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06520-8020, USA.ORCID 0000-0001-6973-5679
Rebecca SullivanDepartment of Medicine, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06520-8020, USA.
Stephen ParzialeYale Center for Analytical Sciences, Yale School of Public Health, New Haven, CT 06510, USA.ORCID 0009-0001-5074-1822
Yanhong DengYale Center for Analytical Sciences, Yale School of Public Health, New Haven, CT 06510, USA.ORCID 0000-0002-4333-468X
Diana CarranoRehabilitation Supervisor, Yale New Haven Hospital, New Haven, CT 06510, USA.
Christine SimpsonDepartment of Medicine, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06520-8020, USA.
Sylvie DufourDepartment of Medicine, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06520-8020, USA.
Thomas CarpenterDepartment of Pediatrics, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06510, USA.
Kitt Falk PetersenDepartment of Medicine, Section of Endocrinology, Yale School of Medicine, New Haven, CT 06520-8020, USA.

Funding

Yale Clinical and Translational Science Award (U Component)UL1TR001863 · NCATS · YALE UNIVERSITY · PI John H. Krystal, LUCILA OHNO-MACHADO · 2016 to 2026
$102.9M
Yale Diabetes Research CenterP30DK045735 · NIDDK · YALE UNIVERSITY · PI GERALD I SHULMAN · 1993 to 2026
$44.0M
Effects of Hepatic Acetyl-CoA Carboxylase Inhibition on NAFLD and Hepatic Insulin ResistanceR01DK113984 · NIDDK · YALE UNIVERSITY · PI SHULMAN, GERALD I · 2017 to 2021
$3.7M
Targeting hepatic mitochondrial oxidation to treat NAFLD, NASH and type 2 diabetesR01DK135645 · NIDDK · YALE UNIVERSITY · PI KITT F PETERSEN, GERALD I SHULMAN · 2024 to 2026
$2.1M
NCATS NIH HHS UL1 TR001863NIDDK NIH HHS P30 DK045735NIDDK NIH HHS R01 DK113984NIDDK NIH HHS R01 DK135645Ultragenyx UX023-IST033
6 · The paper itself

Abstract

contextIn clinical trials, burosumab ameliorates symptoms of pain, fatigue, and stiffness and improves performance on certain muscle function studies in patients with X-linked hypophosphatemia (XLH).

objectiveThis work aimed to determine if burosumab increases adenosine triphosphate (ATP) synthesis in skeletal muscle of treatment-naive adults with XLH, and if so, whether that correlates with improved muscle function.

methodsTen untreated, symptomatic adults with XLH had ATP synthesis rates measured in the right calf using the 31P magnetic resonance spectroscopy saturation transfer technique. Baseline muscle function tests and symptoms of pain, fatigue, stiffness, and lower-extremity joint pain were quantified. All participants were treated with burosumab, 1 mg/kg every 4 weeks for 12 weeks. ATP synthesis rates and muscle function tests were repeated 2 weeks ("peak") and 4 weeks ("trough") after the third dose of burosumab.

resultsAll symptoms improved with treatment. Performance on the 6-Minute Walk Test (6MWT) and Sit to Stand (STS) tests also improved. Muscle strength and ATP synthesis rates did not change over the 3 months of the study. When individuals whose performances on the 6MWT and STS test were at or better than the median outcome for those tests were compared to those whose outcomes were below the median, no difference was observed in the rate of change in ATP synthesis. Intracellular muscle concentrations of phosphate were normal.

conclusionThe improvement in the 6MWT and STS test without changes in muscle strength or ATP synthesis rates suggests that reductions in pain, fatigue, and stiffness may partly explain the improved performance. Intracellular phosphate in skeletal muscle is insulated from hypophosphatemia in XLH.

Indexed as

Antibodies, MonoclonalAntibodies, Monoclonal, HumanizedFamilial Hypophosphatemic RicketsAdenosine TriphosphateAdultFatigueHumansLegMuscle, SkeletalPainPolyphosphatesAdenosine TriphosphateAntibodies, MonoclonalAntibodies, Monoclonal, HumanizedburosumabPolyphosphatestriphosphoric acidburosumabmuscle ATP synthesismuscle functionX-linked hypophosphatemia

Identifiers

PMID37930769
PMCPMC12102717

What Socratic holds

Textmetadata
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.