Evidence map›Paper›PMID 39175217›Full record

Trial reportClinical and translational science2024

Novel cathepsin C inhibitor, BI 1291583, intended for treatment of bronchiectasis: Phase I characterization in healthy volunteers.

Philipp Badorrek, Claudia Diefenbach, Harald Kögler, Anastasia Eleftheraki, Friedeborg Seitz, Jens M Hohlfeld

8 registry-linked trialsAbstract readClinical Trial, Phase IRandomized Controlled Trial
In one paragraph

Trial report in Clinical and translational science, 2024. The graph could read no effect estimate from its abstract, so it casts no vote on the map. It is linked to 8 registered trials, which are not on this map. Cited by 10 papers.

0numbers the graph read from it
0cells of the map it votes in
10citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

NCT03414008 phase1terminatednot on this map

Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Single Rising Oral Doses of BI 1291583 (Single-blind, Partially Randomised, Placebo-controlled Parallel Group Design) in Healthy Male Subjects

TypeinterventionalSponsorBoehringer IngelheimRan2018 to 2019Enrolled54ConditionsHealthyArmsBI 1291583, Matching placebo: Tartaric acid
NCT03837964 phase1completednot on this map

Relative Bioavailability of BI 1291583 Following Oral Administration Under Fed and Fasted Conditions in Healthy Male Subjects (an Open-label, Randomised, Single-dose, Two-period, Two-sequence Crossover Study)

TypeinterventionalSponsorBoehringer IngelheimRan2019 to 2019Enrolled12ConditionsHealthyArmsBI 1291583
NCT03868540 phase1terminatednot on this map

Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Multiple Rising Oral Doses of BI 1291583 qd Versus Placebo in Healthy Male and Female Subjects for 4 Weeks (Single-blind, Partially Randomised, Placebo-controlled Parallel Group Design)

TypeinterventionalSponsorBoehringer IngelheimRan2019 to 2019Enrolled24ConditionsHealthyArmsBI 1291583, Placebo
NCT03890887 phase1completednot on this map

Relative Bioavailability of a Single Oral Dose of BI 1291583 When Administered Alone or in Combination With Multiple Oral Doses of Itraconazole in Healthy Male Subjects (an Open-label, Two-period, Fixed Sequence Study)

TypeinterventionalSponsorBoehringer IngelheimRan2019 to 2019Enrolled14ConditionsHealthyArmsBI 1291583, Itraconazole
NCT04866160 phase1completednot on this map

Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Multiple Rising Oral Doses of BI 1291583 qd Versus Placebo in Healthy Male and Female Subjects for 4 Weeks (Single-blind, Partially Randomised, Placebo-controlled Parallel Group Design)

TypeinterventionalSponsorBoehringer IngelheimRan2021 to 2021Enrolled24ConditionsHealthyArmsBI 1291583, Placebo
NCT05238675 phase2completednot on this map

A Randomised, Double-blind, Placebo-controlled, Parallel Group, Dose-finding Study Evaluating Efficacy, Safety and Tolerability of BI 1291583 qd Over at Least 24 Weeks in Patients With Bronchiectasis (AirleafTM)

TypeinterventionalSponsorBoehringer IngelheimRan2022 to 2024Enrolled322ConditionsBronchiectasisArmsBI 1291583, Placebo
NCT05846230 phase2active not recruitingnot on this map

A Randomised, Double-blind, Parallel Group, Roll-over Study Evaluating Long-term Safety and Efficacy of Oral Doses of BI 1291583 q.d. in Patients With Bronchiectasis (Clairleafᵀᴹ)

TypeinterventionalSponsorBoehringer IngelheimRan2023 to 2027Enrolled268ConditionsBronchiectasisArmsBI 1291583, Placebo matching BI 1291583
NCT05865886 phase2completednot on this map

A Randomized, Double-blind, Placebo-controlled, Parallel Group Trial Evaluating Safety, Tolerability, Pharmacodynamics and Pharmacokinetics of BI 1291583 One Tablet Once Daily Over 12 Weeks Versus Placebo in Adult Patients With Cystic Fibrosis Bronchiectasis (Clairafly™)

TypeinterventionalSponsorBoehringer IngelheimRan2024 to 2024Enrolled22ConditionsCystic Fibrosis, BronchiectasisArmsBI 1291583, Placebo to BI 1291583
3 · Its place in the literature

Who cites it

10 citing papers in PubMed.

  1. Trial
  2. Trial
  3. Article
  4. Review
  5. Review
  6. Review
  7. Review
  8. Review
  9. Targeting neutrophil serine proteases in bronchiectasis.The European respiratory journal · 2025
    Review
  10. Neutrophil serine proteases in cystic fibrosis: role in disease pathogenesis and rationale as a therapeutic target.European respiratory review : an official journal of the European Respiratory Society · 2024
    Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

6 authors.

Philipp BadorrekDepartment of Clinical Airway Research, Fraunhofer Institute for Toxicology and Experimental Medicine (ITEM), Hannover, Germany.
Claudia DiefenbachBoehringer Ingelheim Pharma GmbH & Co. KG, Biberach, Germany.
Harald KöglerBoehringer Ingelheim International GmbH, Ingelheim, Germany.
Anastasia EleftherakiBoehringer Ingelheim Pharma GmbH & Co. KG, Biberach, Germany.
Friedeborg SeitzClinical Research Services, Mannheim, Germany.ORCID 0000-0002-4460-5867
Jens M HohlfeldDepartment of Clinical Airway Research, Fraunhofer Institute for Toxicology and Experimental Medicine (ITEM), Hannover, Germany.ORCID 0000-0003-2646-6186

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Novel treatments are needed to reduce inflammation, improve symptoms, address exacerbations, and slow disease progression in bronchiectasis. Cathepsin C (CatC) inhibition promises to achieve this through reduction of neutrophil-derived serine protease (including neutrophil elastase [NE] and proteinase 3 [PR3]) activation. Here, we present the phase I characterization of the novel CatC inhibitor, BI 1291583. Five phase I trials of BI 1291583 in healthy subjects are presented: a single-rising-dose study (NCT03414008) and two multiple-rising-dose studies (NCT03868540 and NCT04866160) assessing the safety, tolerability, pharmacodynamics, and pharmacokinetics of BI 1291583; a food effect study (NCT03837964); and a drug-drug interaction study (NCT03890887) of BI 1291583 and itraconazole. BI 1291583 was safe and well tolerated across the doses tested in these trials. Most adverse events (AEs) were mild or moderate in intensity, with no serious AEs, AEs of special interest or deaths reported in any trial. Drug-related skin exfoliation was not reported more frequently in subjects treated with BI 1291583 compared with placebo. BI 1291583 was readily absorbed, and pharmacokinetics were supra-proportional over the dose ranges assessed. Additionally, BI 1291583 inhibited CatC in a dose-dependent manner, inhibited downstream NE activity, and decreased PR3 levels. No food effect was observed. Co-administration of multiple doses of itraconazole increased BI 1291583 exposure approximately twofold. Due to these promising phase I results, a multinational phase II program of BI 1291583 in adults with bronchiectasis is ongoing (Airleaf™ [NCT05238675], Clairafly™ [NCT05865886], and Clairleaf™ [NCT05846230]).

Indexed as

BronchiectasisCathepsin CHealthy VolunteersAdolescentAdultDose-Response Relationship, DrugDouble-Blind MethodDrug InteractionsFemaleFood-Drug InteractionsHumansItraconazoleMaleMiddle AgedYoung AdultCathepsin CCTSC protein, humanItraconazole

Identifiers

PMID39175217
PMCPMC11341832

What Socratic holds

Textmetadata
LicenceCC BY-NC
Read underepoch 390

Registered trials

and 2 more above

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.