Evidence mapPaperPMID 39231891Full record

ArticleThe AAPS journal2024

A Risk-Based Assessment for Determining the Pharmacokinetic Comparability Requirements of Biologic-Device Combination Products Administered by Subcutaneous Injection.

Mark Klitgaard Nøhr, Shaik Rizwan Waheed, Rasmus Juul Kildemoes, Vibeke Hatorp, Tine Aggerholm Bækdal, Charlotte Lindorff Adrian, Lars Peter Korsholm, Eva Lisby Arp-Hansen, Helle Holst, Scott W Roberts

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Article in The AAPS journal, 2024. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 1 paper.

0numbers the graph read from it
0cells of the map it votes in
1citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

1 citing paper in PubMed.

  1. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

10 authors.

Mark Klitgaard NøhrRegulatory Affairs, Chemistry, Manufacturing and Controls, Novo Nordisk A/S, Søborg, Denmark.
Shaik Rizwan WaheedRegulatory Affairs, Device, Novo Nordisk A/S, Søborg, Denmark.
Rasmus Juul KildemoesMedical & Science Clinical Pharmacology, Novo Nordisk A/S, Søborg, Denmark.
Vibeke HatorpMedical & Science Clinical Pharmacology, Novo Nordisk A/S, Søborg, Denmark.
Tine Aggerholm BækdalMedical & Science Clinical Pharmacology, Novo Nordisk A/S, Søborg, Denmark.
Charlotte Lindorff AdrianMedical & Science Clinical Pharmacology, Novo Nordisk A/S, Søborg, Denmark.
Lars Peter KorsholmBiostatistics Research and Development, Novo Nordisk A/S, Søborg, Denmark.
Eva Lisby Arp-HansenGlobal Regulatory Affairs, Novo Nordisk A/S, Søborg, Denmark.
Helle HolstMedical & Science Rare Endocrine Disorders, LCM & Cell Therapies, Novo Nordisk A/S, Søborg, Denmark.
Scott W RobertsRegulatory Affairs, Chemistry, Manufacturing and Controls, Novo Nordisk A/S, Søborg, Denmark. osrb@novonordisk.com.ORCID 0000-0001-8963-3282

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

The development of new large molecule drug therapies along with the innovation of biologic-device combination products such as prefilled syringes, autoinjectors and pen injectors have significantly impacted the treatment of new diseases and has improved the process of administering parenteral medicines. To support the regulatory approval of a new biologic-device combination products or subsequent chemistry, manufacturing and control changes impacting a combination product, sponsor companies must thoroughly assess the potential impact to product quality, safety and efficacy. In this report, a risk-based process to determine the potential impact to product quality, safety, and efficacy as well as corresponding regulatory actions supporting a chemistry, manufacturing and control change is presented. The risk assessment includes the standardized assessment of a) chemistry, manufacturing and control risk factors, potential responses and appropriately weighted scoring; b) pharmacokinetic risk factors, potential responses and appropriately weighted scoring; and c) the use of a 2-dimensional risk grid to combine the chemistry, manufacturing and control risks and pharmacokinetic risks to provide a regulatory recommendation. Three case studies (two clinical case studies and a post-approval case study) are provided to demonstrate the assessment process and capabilities.

Indexed as

Biological ProductsHumansInjections, SubcutaneousRisk AssessmentRisk FactorsBiological Productsbiologic-device combination productpharmacokinetic comparabilitysubcutaneous administration

Identifiers

What Socratic holds

Textmetadata
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.