Evidence map›Paper›PMID 39597922›Full record

ArticleJournal of clinical medicine2024

German Real-World Experience of Patients with Diverse Features of Acute Intermittent Porphyria Treated with Givosiran.

Ilja Kubisch, Nils Wohmann, Thaddäus Till Wissniowski, Thomas Stauch, Lucienne Oettel, Eva Diehl-Wiesenecker, Rajan Somasundaram, Ulrich Stölzel

Abstract read
In one paragraph

Article in Journal of clinical medicine, 2024. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 5 papers.

0numbers the graph read from it
0cells of the map it votes in
5citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

5 citing papers in PubMed.

  1. Article
  2. Review
  3. Review
  4. A Prospective, Blinded Study of Symptom Prevalence and Specificity of Porphyrin Precursors in Carriers of Acute Hepatic Porphyria.Liver international : official journal of the International Association for the Study of the Liver · 2025
    Article
  5. Acute hepatic porphyrias.Porto biomedical journal
    Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors.

Ilja KubischPorphyria Center, Chemnitz Hospital, 09116 Chemnitz, Germany.
Nils WohmannPorphyria Center, Chemnitz Hospital, 09116 Chemnitz, Germany.
Thaddäus Till WissniowskiPorphyria Center, Chemnitz Hospital, 09116 Chemnitz, Germany.
Thomas StauchMVZ Labor Volkmann, 76131 Karlsruhe, Germany.ORCID 0000-0002-1622-4901
Lucienne OettelPorphyria Center, Chemnitz Hospital, 09116 Chemnitz, Germany.
Eva Diehl-WieseneckerDepartment of Emergency Medicine and Porphyria Clinic, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, 10115 Berlin, Germany.ORCID 0000-0002-4058-9337
Rajan SomasundaramDepartment of Emergency Medicine and Porphyria Clinic, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, 10115 Berlin, Germany.
Ulrich StölzelPorphyria Center, Chemnitz Hospital, 09116 Chemnitz, Germany.ORCID 0009-0008-4050-658X

Funding

Alnylam Germany GmbH; Erika-Mann-Str. 7; D-80636 Munich. NA
6 · The paper itself

Abstract

PubMed holds no abstract for this paper.

Indexed as

AHPAIPALAALAS1chronic symptomsfatigueFatigue Assessment Scale (FAS)givosiranHR-QoLIpnetPBGsiRNAsporadic attack

Identifiers

PMID39597922
PMCPMC11594983

What Socratic holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.