Evidence map›Paper›PMID 39808408›Full record

Trial reportTargeted oncology2025

Buparlisib and Paclitaxel in Patients with Head and Neck Squamous Cell Carcinoma: Immunogenomic Biomarkers of Efficacy from the BERIL-1 Study.

Antoine Desilets, Justin Lucas, Lisa F Licitra, Sunny Lu, Archie Tse, Tom Tang, Kevin Dreyer, Nanhai He, Lars E Birgerson, Sandrine Faivre and 1 more

Registry-linked trialAbstract readRandomized Controlled TrialClinical Trial, Phase II
PubMed Publisher
In one paragraph

Trial report in Targeted oncology, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. It is linked to trial NCT01852292 (Double Blind, Placebo Controlled Study Assessing the Efficacy of Buparlisib), which is not on this map. Cited by 6 papers.

0numbers the graph read from it
0cells of the map it votes in
6citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

NCT01852292 phase2terminatednot on this map

Double Blind, Placebo Controlled Study Assessing the Efficacy of Buparlisib (BKM120) Plus Paclitaxel Versus Placebo Plus Paclitaxel in Patients With Platinum Pre-treated Recurrent or Metastatic Head and Neck Squamous Cell Carcinoma (HNSCC)

TypeinterventionalSponsorNovartis PharmaceuticalsRan2013 to 2017Enrolled157ConditionsHead and Neck Squamous Cell CarcinomaArmsBuparlisib, Buparlisib matching Placebo, Paclitaxel
3 · Its place in the literature

Who cites it

6 citing papers in PubMed.

  1. Article
  2. Review
  3. Article
  4. Article
  5. Article
  6. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

11 authors.

Antoine DesiletsHematology-Oncology Service, Department of Medicine, Centre hospitalier de l'Université de Montréal (CHUM), 1000, rue Saint-Denis, Montreal, QC, Canada. antoine.desilets@umontreal.ca.ORCID http://orcid.org/0000-0002-9382-7597
Justin LucasAdlai Nortye, North Brunswick, NJ, USA.
Lisa F LicitraHead and Neck Cancer Medical Oncology 3 Unit, Fondazione IRCCS Istituto Nazionale dei Tumori, Department of Oncology and Hemato-Oncology, University of Milan, Milan, Italy.
Sunny LuAdlai Nortye, North Brunswick, NJ, USA.
Archie TseAdlai Nortye, North Brunswick, NJ, USA.
Tom TangAdlai Nortye, North Brunswick, NJ, USA.
Kevin DreyerAdlai Nortye, North Brunswick, NJ, USA.
Nanhai HeAdlai Nortye, North Brunswick, NJ, USA.
Lars E BirgersonAdlai Nortye, North Brunswick, NJ, USA.
Sandrine FaivreHôpital St-Louis, Paris, France.
Denis SoulièresHematology-Oncology Service, Department of Medicine, Centre hospitalier de l'Université de Montréal (CHUM), 1000, rue Saint-Denis, Montreal, QC, Canada.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

backgroundBERIL-1 was a randomized phase 2 study that studied paclitaxel with either buparlisib, a pan-class I PIK3 inhibitor, or placebo in patients with recurrent or metastatic (R/M) head and neck squamous cell cancer (HNSCC). Considering the therapeutic paradigm shift with immune checkpoint inhibitors (ICIs) now approved in the first-line setting, we present an updated immunogenomic analysis of patients enrolled in BERIL-1, including patients with immune-infiltrated tumors.

objectiveThe objective of this study was to identify biomarkers predictive of treatment efficacy in the context of the post-ICI therapeutic landscape. PATIENTS AND

methodsGenomic analyses were performed at baseline on tumor and/or plasma circulating DNA (ctDNA) samples, and immunohistochemistry (IHC) studies, including immune infiltration [tumor-infiltrating lymphocytes (TILs) and CD8 expression], were performed on tumor samples. Immunogenomic biomarkers were correlated to overall survival (OS).

resultsAmong 158 patients enrolled in BERIL-1, either tumor (53.2%; n = 84) or ctDNA samples (70.8%; n = 112) were available in 85.4% (n = 135). The most commonly mutated genes were TP53 (57.0%), NOTCH1 (23.7%), and PIK3CA (22.2%). In the IHC studies, 98.6% (n = 68/69) of patients were TILs positive in the buparlisib arm versus 94.4% (n = 68/72) in the placebo arm. In patients with TILs-positive tumors, enrichment for clinical benefit on the buparlisib arm was seen in those with PIK3 pathway activation [25.0% (n = 17/68)] with a hazard ratio (HR) for death of 0.43 [95% confidence interval (CI) 0.21-0.87, p = 0.016]. Similarly, improved OS was seen in patients on the buparlisib arm and NOTCH pathway activation [20.5% (n = 14/68)] with a HR for death of 0.40 (95% CI 0.18-0.90, p = 0.022). Both associations were absent in the placebo group. TP53 and tumor mutational burden (TMB) did not correlate with OS in the buparlisib or placebo arms.

conclusionsIn this immunogenomic analysis of BERIL-1, improved HRs for OS were seen in patients with tumor immune infiltration and selected oncogenic alterations, including PIK3 and NOTCH pathway activation (NCT01852292).

Indexed as

AminopyridinesAntineoplastic Combined Chemotherapy ProtocolsBiomarkers, TumorHead and Neck NeoplasmsMorpholinesPaclitaxelSquamous Cell Carcinoma of Head and NeckAdultAgedFemaleHumansMaleMiddle AgedAminopyridinesBiomarkers, TumorMorpholinesNVP-BKM120Paclitaxel

Identifiers

What Socratic holds

Textmetadata
Read underepoch 390

Registered trials

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.