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ArticleJournal of neurology2025

Multi-omics profiling in spinal muscular atrophy (SMA): investigating lipid and metabolic alterations through longitudinal CSF analysis of Nusinersen-treated patients.

Martina Zandl-Lang et al.PubMed ↗Full text ↗Publisher ↗

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10 papers cite it

2025
2026
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Full record →Abstract, authors, funding and every citing paper · PMID 39904776