Evidence mapPaperPMID 40528034Full record

ReviewActa pharmacologica Sinica2025

Advancing active compound discovery for novel drug targets: insights from AI-driven approaches.

Xing-You Wang, Yang Chen, Yu-Fan Li, Chao-Yang Wei, Meng-Ya Liu, Chen-Xing Yuan, Yao-Yu Zheng, Mo-Han Qin, Yu-Feng Sheng, Xiao-Chu Tong and 2 more

Abstract readReview
In one paragraph

Review in Acta pharmacologica Sinica, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 3 papers.

0numbers the graph read from it
0cells of the map it votes in
3citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

3 citing papers in PubMed.

  1. Review
  2. Primary Metabolites in ThreeLife (Basel, Switzerland) · 2026
    Article
  3. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

12 authors.

Xing-You Wang *Drug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Yang Chen *Drug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Yu-Fan LiDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Chao-Yang WeiDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Meng-Ya LiuDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Chen-Xing YuanDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Yao-Yu ZhengDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Mo-Han QinDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Yu-Feng ShengDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Xiao-Chu TongDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China.
Ming-Yue ZhengDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China. myzheng@simm.ac.cn.ORCID http://orcid.org/0000-0002-3323-3092
Xu-Tong LiDrug Discovery and Design Center, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica Chinese Academy of Sciences, Shanghai, 201203, China. lixutong@simm.ac.cn.ORCID http://orcid.org/0000-0001-9547-0643

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

The discovery of active compounds for novel, underexplored targets is essential for advancing innovative therapeutics across a wide range of diseases. Recent advancements in artificial intelligence (AI) are revolutionizing active compound discovery by dramatically enhancing the efficiency, accuracy, and scalability previously challenged by traditional methods. This review provides a comprehensive overview of AI-driven methodologies for active compound discovery, with a particular focus on their application to novel targets. Initially, we explore how AI overcomes traditional bottlenecks in molecular design, enabling precise protein perception through high-accuracy protein structure prediction and enhanced docking precision. Building upon these target-focused capabilities, AI-driven approaches also advance ligand exploration, effectively bridging biological and chemical spaces through sophisticated data transfer techniques that maximize the utility of available activity data. By assessing overall cellular or organismal responses, AI plays a pivotal role in decoding complex biological systems, driving phenotypic drug discovery (PDD) through multi-modal data integration. Finally, we discuss how AI is addressing challenges associated with targeting previously undruggable proteins, exemplified by the development of protein degraders. By synthesizing these cutting-edge advancements, this review serves as a valuable resource for researchers seeking to leverage AI in the discovery of next-generation therapeutics.

Indexed as

Artificial IntelligenceDrug DiscoveryAnimalsDrug DesignHumansLigandsProteinsLigandsProteinsAI-driven drug discoveryligand explorationmolecular designnovel drug targetsphenotypic drug discoveryundruggable targets

Identifiers

PMID40528034
PMCPMC12552591

What Socratic holds

Textmetadata
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.