Evidence mapPaperPMID 40741268Full record

ArticleArchives of medical science : AMS2025

Lipoprotein lipase deficiency: heterozygotes match homozygotes in severity.

Dominika Szczęśniak, Małgorzata Bednarska-Makaruk, Olga Drgas, Karolina Kowalczyk, Magdalena M Kacprzak, Paweł Aleksandrowicz, Lidia Kotuła, Magdalena Mroczek

Abstract read
In one paragraph

Article in Archives of medical science : AMS, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 2 papers.

0numbers the graph read from it
0cells of the map it votes in
2citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

2 citing papers in PubMed.

  1. Review
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4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors.

Dominika SzczęśniakDepartment of Genetics, Institute Psychiatry and Neurology, Warsaw, Poland.
Małgorzata Bednarska-MakarukDepartment of Genetics, Institute Psychiatry and Neurology, Warsaw, Poland.
Olga DrgasMedGen Medical Center, Warsaw, Poland.
Karolina KowalczykMedGen Medical Center, Warsaw, Poland.
Magdalena M KacprzakMedGen Medical Center, Warsaw, Poland.
Paweł AleksandrowiczDepartment of Dental Surgery, Medical University of Warsaw, Poland.
Lidia KotułaDepartment of Genetics, Medical University of Lublin, Lublin, Poland.
Magdalena MroczekDepartment of Neurology, University Hospital Basel, University of Basel, Basel, Switzerland.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Introduction: Biallelic pathogenic variants in the Material and methods: Genetic data were derived from a Polish cohort of 5623 whole exome sequenced patients. In 52 cases the indication for WES genetic testing was "hypertriglyceridemia '' and for 5571 there was another clinical indication, mainly autism spectrum disorder, dysmorphia and neurodegenerative diseases. Results: We present 22 heterozygous and 2 homozygous/compound heterozygous individuals for the pathogenic/likely pathogenic LPL variant and describe HTG levels, phenotypic manifestations and age of onset in the context of molecular findings where available. We report for the first time heterozygous LPL individuals with very severe HTG (TG ≥ 22.6 mmol/l; > 2000 mg/dl) and additional symptoms such as pancreatitis and recurrent abdominal pain. Conclusions: We argue that although the individuals carrying the single LPL pathogenic/likely pathogenic variant display the whole disease spectrum, the severe phenotype of heterozygotes with dominantly inherited LPL-related HTG may also exist.

Indexed as

autosomal dominantco-dominancefamilial chylomicronemia syndromehypertriglyceridemialipoprotein lipase

Identifiers

PMID40741268
PMCPMC12305545

What Socratic holds

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Registered trials

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.