Evidence mapPaperPMID 41039909Full record

ArticleClinical and translational science2025

Real-World Evaluation of Outcomes and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Pediatric Patients With Cystic Fibrosis: A Retrospective Study.

Nicola Perrotta, Luigi Angelo Fiorito, Rossella Gentile, Roberta Vescovo, Alfonso Piciocchi, Patrizia Troiani, Roberto Poscia, Giuseppe Cimino

Abstract read
In one paragraph

Article in Clinical and translational science, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 4 papers.

0numbers the graph read from it
0cells of the map it votes in
4citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

4 citing papers in PubMed.

  1. Article
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4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors.

Nicola PerrottaDepartment of Physiology and Pharmacology "V. Erspamer", Sapienza University, Rome, Italy.ORCID 0000-0002-0809-5118
Luigi Angelo FioritoDepartment of Physiology and Pharmacology "V. Erspamer", Sapienza University, Rome, Italy.
Rossella GentileDepartment of Physiology and Pharmacology "V. Erspamer", Sapienza University, Rome, Italy.
Roberta VescovoDepartment of Chemistry and Technology of Drugs, Sapienza University, Rome, Italy.
Alfonso PiciocchiBiostatistics Unit, GIMEMA Foundation, Rome, Italy.
Patrizia TroianiRegional Cystic Fibrosis Center, AOU Policlinico Umberto I - Sapienza University, Rome, Italy.
Roberto PosciaClinical Research Unit, AOU Policlinico Umberto I - Sapienza University, Rome, Italy.
Giuseppe CiminoRegional Cystic Fibrosis Center, AOU Policlinico Umberto I - Sapienza University, Rome, Italy.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Elexacaftor/Tezacaftor/Ivacaftor (ETI) therapy has significantly improved clinical outcomes in people with cystic fibrosis (PwCF) carrying at least one Phe508del CFTR mutation. However, real-world evidence on the safety and effectiveness of ETI in pediatric populations remains limited, particularly in children with more severe disease phenotypes who are often excluded from clinical trials. We analyzed clinical, functional, and microbiological data from pediatric CF patients aged 6-17 years treated with ETI between October 2022 and March 2024. Lung function (ppFEV

Indexed as

AminophenolsBenzodioxolesCystic FibrosisIndolesPyrazolesPyridinesQuinolonesAdolescentChildChloride Channel AgonistsCystic Fibrosis Transmembrane Conductance RegulatorDrug CombinationsFemaleHumansMaleQuality of LifeAminophenolsBenzodioxolesCFTR protein, humanChloride Channel AgonistsCystic Fibrosis Transmembrane Conductance RegulatorDrug CombinationsIndolesivacaftorPyrazolesPyridinesQuinolonescystic fibrosiseffectivenesselexacaftor‐tezacaftor‐ivacaftorpediatric settingsafety

Identifiers

PMID41039909
PMCPMC12491836

What Socratic holds

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LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.