Evidence mapPaperPMID 41125751Full record

ArticleScientific reports2025

Erdafitinib suppresses pathological retinal angiogenesis via dual targeting of FGFR and VEGFR2 signaling.

Yingli Mo, Bei Lu, Yuping Xu, Xiaojuan Fan, Qingshuang Zhang, Shaowu Cheng, Lu Tang, Qinghua Peng

Abstract read
In one paragraph

Article in Scientific reports, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 1 paper.

0numbers the graph read from it
0cells of the map it votes in
1citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

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Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

1 citing paper in PubMed.

  1. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors.

Yingli MoHunan Provincial Key Laboratory of TCM Diagnostics, Hunan University of Chinese Medicine, Changsha, 410208, Hunan, China.
Bei LuHunan Provincial Key Laboratory of TCM Diagnostics, Hunan University of Chinese Medicine, Changsha, 410208, Hunan, China.
Yuping XuSchool of Medicine, Yiyang Medical College, Yingbin Road 516, Yiyang, 413000, Hunan, China.
Xiaojuan FanSchool of Nursing, Yiyang Medical College, Yingbin Road 516, Yiyang, 413000, Hunan, China.
Qingshuang ZhangHunan Provincial Key Laboratory of TCM Diagnostics, Hunan University of Chinese Medicine, Changsha, 410208, Hunan, China.
Shaowu ChengSchool of Integrated Chinese and Western Medicine, Hunan University of Chinese Medicine, Changsha, 410208, Hunan, China.
Lu TangDepartment of Cardiology, Yiyang Central Hospital, Kangfu North Road 118, Yiyang, 413000, Hunan, China. 150556119@qq.com.
Qinghua PengHunan Provincial Key Laboratory of TCM Diagnostics, Hunan University of Chinese Medicine, Changsha, 410208, Hunan, China. pengqinghua@hnucm.edu.cn.

Funding

China Postdoctoral Fellowship Program 2020M672502Hunan Provincial Department of Education, Open Fund for First-Class Disciplines at Hunan University of Chinese Medicine 2021ZYX10Natural Science Foundation of Hunan Province 2022JJ50039Yiyang Science and Technology Innovation Plan Project 2024YR28
6 · The paper itself

Abstract

Pathological retinal angiogenesis drives vision loss in diseases like proliferative diabetic retinopathy (PDR) and retinal vein occlusion (RVO). Erdafitinib, a pan-fibroblast growth factor receptor (FGFR) inhibitor, has shown therapeutic potential in FGFR-mutated urothelial carcinoma. This study aimed to determine whether erdafitinib suppresses pathological retinal angiogenesis beyond its canonical FGFR inhibition, and to dissect its potential mechanisms through multi-model validation. We employed zebrafish developmental angiogenesis and oxygen-induced retinopathy (OIR) mouse models, combined with in vitro endothelial cell assays. In zebrafish, erdafitinib dose-dependently inhibited intersegmental vessel (ISV) formation and disrupted retinal angiogenesis, with confocal microscopy revealing truncated vascular length (by 62% at 4 µM vs. controls). The OIR model demonstrated erdafitinib's efficacy in reducing neovascular density (35% decrease) and pathological tuft formation. Mechanistically, erdafitinib impaired human umbilical vein endothelial cell (HUVEC) tube formation and migration, accompanied by downregulation of VEGFR2 expression (2.1-fold reduction) and inhibition of AKT/ERK phosphorylation. Molecular docking confirmed erdafitinib's binding to VEGFR2 kinase domain (binding energy: -7.8 kcal/mol), albeit with lower affinity than FGFR1 (-10.2 kcal/mol). These findings establish that erdafitinib exerts off-target anti-angiogenic effects by blocking VEGFR2 phosphorylation and downstream signaling, supporting its repurposing potential for anti-VEGF-resistant retinal vascular diseases. Further studies should address its intraocular pharmacokinetics and long-term safety.

Indexed as

Neovascularization, PathologicPyrazolesQuinoxalinesReceptors, Fibroblast Growth FactorRetinal NeovascularizationSignal TransductionVascular Endothelial Growth Factor Receptor-2AngiogenesisAngiogenesis InhibitorsAnimalsCell MovementDisease Models, AnimalHumansHuman Umbilical Vein Endothelial CellsMiceMolecular Docking SimulationAngiogenesis InhibitorserdafitinibPyrazolesQuinoxalinesReceptors, Fibroblast Growth FactorVascular Endothelial Growth Factor Receptor-2AKT/ERK signalingErdafitinibOxygen-induced retinopathy (OIR) modelRetinal angiogenesisVEGFR2Zebrafish

Identifiers

PMID41125751
PMCPMC12546633

What Socratic holds

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LicenceCC BY-NC-ND
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Registered trials

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.