Evidence mapPaperPMID 41361659Full record

ArticleActa pharmacologica Sinica2026

Modest improvement of metabolic and behavioral deficits with long-term ambroxol treatment in a Pink1

Luisa Franck, Lucie Valek, Lisa Hahnefeld, Sandra Trautmann, Carlo Angioni, Marc-Philipp Weyer, Dominique Thomas, Robert Gurke, Ilka Wittig, Gerd Geisslinger and 1 more

Abstract read
In one paragraph

Article in Acta pharmacologica Sinica, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 1 paper.

0numbers the graph read from it
0cells of the map it votes in
1citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

1 citing paper in PubMed.

  1. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

11 authors.

Luisa FranckInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Lucie ValekInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Lisa HahnefeldInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Sandra TrautmannInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Carlo AngioniInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Marc-Philipp WeyerInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Dominique ThomasInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Robert GurkeInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Ilka WittigFunctional Proteomics, Institute of Cardiovascular Physiology, Goethe-University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Gerd GeisslingerInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany.
Irmgard TegederInstitute of Clinical Pharmacology, Goethe University Frankfurt, Faculty of Medicine, Frankfurt am Main, Germany. tegeder@em.uni-frankfurt.de.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Parkinson's disease (PD) involves α-synuclein (αSyn) oligomerization and aggregation, processes facilitated by glycosphingolipids. Defective glycosphingolipid transport and degradation-especially via the lipid-degrading enzyme glucocerebrosidase 1 (GCase, gene GBA1)-aggravate PD and increase dementia risk. Ambroxol is a mucolytic drug and has emerged as a promising add-on therapy for PD since it acts as a chaperone for misfolded GCase, thereby increases the likelihood that mutated and misfolded GCase eludes ER-associated degradation (ERAD) and is transported to its destination, the lysosome. In this study we investigated whether and how ambroxol provided therapeutic benefits for PD irrespective of the GBA1 mutation status. Pink1

Indexed as

alpha-SynucleinAmbroxolParkinson DiseaseProtein KinasesAnimalsBehavior, AnimalDisease Models, AnimalGlucosylceramidaseMaleMiceMice, Inbred C57BLMutationalpha-SynucleinAmbroxolGlucosylceramidaseProtein KinasesSnca protein, mouseambroxolglucocerebrosidase 1lipidomic and metabolomic analyseslysosomesParkinson’s diseaseα-synuclein

Identifiers

PMID41361659
PMCPMC13018195

What Socratic holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.