Evidence mapPaperPMID 41555430Full record

ReviewOrphanet journal of rare diseases2026

Decoding rare inherited metabolic disorders: advancing precision in screening and diagnosis.

Muhammad Wasim, Haq Nawaz Khan, Yajun Wang, Guoda Ma

Abstract readReview
In one paragraph

Review in Orphanet journal of rare diseases, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

0numbers the graph read from it
0cells of the map it votes in
0citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

4 authors.

Muhammad WasimMaternal and Children's Health Research Institute, Shunde Women and Children's Hospital, Guangdong Medical University, Foshan, 528300, China. mm.waseemjee@gmail.com.ORCID http://orcid.org/0000-0003-0969-6609
Haq Nawaz KhanPathology and Laboratory Medicine, The Aga Khan University, Karachi, 74800, Pakistan.
Yajun WangInstitute of Pediatrics, Shunde Women and Children's Hospital, Guangdong Medical University, Foshan, 528300, China.
Guoda MaMaternal and Children's Health Research Institute, Shunde Women and Children's Hospital, Guangdong Medical University, Foshan, 528300, China.

Funding

Guangdong Medical Research Foundation 2024BSHQD002
6 · The paper itself

Abstract

Inherited Metabolic Disorders (IMDs) constitute a varied group of genetic disorders marked by disruptions in essential molecule metabolism, resulting in diverse clinical manifestations. Early diagnosis and prompt intervention are critical for optimal disease management and the prevention of long-term complications. Metabolomics, an impactful analytical approach, has surfaced as a valuable tool in the screening, diagnosis, and monitoring of IMDs. This review offers an insight into the role of metabolomics in IMD screening, emphasizing its applications, challenges, and future potential. Metabolomics interrogates the complete spectrum of small-molecule metabolites in biological samples, allowing precise detection of metabolic perturbations that serve as signatures of specific disease states. Despite challenges in data interpretation and standardization, the ongoing evolution of technology positions metabolomics as a promising avenue for early detection and personalized management of IMDs, contributing to advancements in both research and clinical practice.

Indexed as

Metabolic DiseasesMetabolism, Inborn ErrorsRare DiseasesHumansMetabolomics

Identifiers

PMID41555430
PMCPMC12896334

What Socratic holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.