Evidence mapPaperPMID 42010184Full record

ArticleTargeted oncology2026

Real-World Outcomes of Ivosidenib in IDH1-Mutant Biliary Tract Cancer: A Multicenter Retrospective Analysis and Comparison with the TrinetX Database.

Lena Dreikhausen, Alexander Olkus, Michael Dill, Christoph Springfeld, Philipp Heumann, Nadine Schulte, Konstantina Atanasova, Matthias P Ebert, Anne Letsch, Anna M Wandmacher and 1 more

Abstract readMulticenter StudyComparative Study
In one paragraph

Article in Targeted oncology, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

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0citing papers in PubMed
field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

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5 · Who and what money

Authors and funding

11 authors.

Lena DreikhausenDepartment of Medicine II, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany. lena.dreikhausen@umm.de.ORCID http://orcid.org/0000-0001-9844-0159
Alexander OlkusDepartment of Gastroenterology, Hepatology, Infectious Diseases and Intoxication, University Hospital Heidelberg, Medical Faculty Heidelberg, Heidelberg University, Heidelberg, Germany.
Michael DillDepartment of Gastroenterology, Hepatology, Infectious Diseases and Intoxication, University Hospital Heidelberg, Medical Faculty Heidelberg, Heidelberg University, Heidelberg, Germany.
Christoph SpringfeldDepartment of Medical Oncology, National Center for Tumor Diseases (NCT), University Hospital Heidelberg, Heidelberg, Germany.
Philipp HeumannDepartment of Internal Medicine I, Gastroenterology, Hepatology, Endocrinology, Rheumatology and Infectious Diseases, University Hospital Regensburg, Regensburg, Germany.
Nadine SchulteDepartment of Medicine II, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany.
Konstantina AtanasovaDepartment of Medicine II, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany.
Matthias P EbertDepartment of Medicine II, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany.
Anne LetschDepartment of Internal Medicine II, University Hospital Center Schleswig-Holstein, Kiel, Germany.
Anna M Wandmacher *Department of Internal Medicine II, University Hospital Center Schleswig-Holstein, Kiel, Germany.
Tianzuo Zhan *Department of Medicine II, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany. Tianzuo.zhan@umm.de.

Funding

Deutsche Forschungsgemeinschaft DFG ZH 1023 (FOR 5806)Deutsche Forschungsgemeinschaft project number 413490537Deutsche Krebshilfe 70113858Medical Faculty Mannheim Clinician Scientist programMedizinischen Fakultät Heidelberg, Universität Heidelberg Clinician Scientist program
6 · The paper itself

Abstract

backgroundIvosidenib is established as targeted therapy in patients with isocitrate dehydrogenase 1 (IDH1)-mutant advanced biliary tract cancer based on results of the phase III ClarIDHy trial. However, data on the efficacy of ivosidenib in real-world cohorts are limited.

objectiveThis retrospective analysis aims to provide data on the efficacy and safety of ivosidenib in biliary tract cancer in a real-world cohort.

methodsPatients with IDH1 mutant biliary tract cancer treated with ivosidenib at four German university medical centers from 2020 to 2024 were retrospectively identified. Clinicopathological parameters and treatment courses were collected. Furthermore, clinical outcomes of patients with biliary tract cancer who received ivosidenib were retrospectively retrieved from the global health network database TriNetX.

resultsIn total, 14 patients who received ivosidenib were identified. Mean age at diagnosis was 61 years and 50% of patients were female. Nine patients had an IDH1 R132C, four an IHD1 R132L, and one an IDH1 R132S mutation. Ten patients received ivosidenib as second-line therapy and four in later lines. Partial response was observed in two patients, stable disease in three, and progressive disease in nine patients. Median progression-free survival was 5.6 months (95% confidence interval 4.3, not estimated) and median overall survival was 12.7 months (95% confidence interval 8.2, not estimated). No discontinuation of ivosidenib because of toxicity was observed. A total of 228 patients were identified in the TriNetX database. Mean age was 64.4 years and 64% of patients were female. Median overall survival in this cohort was 9.6 months (95% confidence interval 8.07, 11.19).

conclusionsReal-world data from our cohort and the TriNetX database support the oncological outcomes reported in the ClarIDHy trial and other real-world cohorts.

Indexed as

Antineoplastic AgentsBiliary Tract NeoplasmsGlycineIsocitrate DehydrogenasePyridinesAgedFemaleHumansMaleMiddle AgedMutationRetrospective StudiesTreatment OutcomeAntineoplastic AgentsGlycineIDH1 protein, humanIsocitrate DehydrogenaseivosidenibPyridines

Identifiers

PMID42010184
PMCPMC13222294

What Socratic holds

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.