27 authors.
Kim Anh VuRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-6030-567X Han ZhangRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0003-1090-2967 Nadia AmraniRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0001-6871-7962 Gitali DeviRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-9080-4656 Nicholas GastonRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-3862-9002 Jonathan LeeRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Stacy A MaitlandDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Zexiang ChenRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Dimas EcheverriaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Pengpeng LiuDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-4891-8780 Karthikeyan PonnienselvanDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-8016-9433 Matthew B HanlonDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Connor LucasRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Kevin LukDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-9727-1960 Jacquelyn SousaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
David CooperRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Alyxandr SrnkaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Julia M Rembetsy-BrownRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.
Aditya Valji AnsodariaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0003-1408-1182 Nathan BamideleRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0001-9051-5531 Aamir MirRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0003-0144-3914 Ken YamadaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-5714-8298 Julia F AltermanRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-6195-0857 Anastasia KhvorovaRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0001-6928-8071 Scot A WolfeDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-7042-201X Erik J SontheimerRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0002-0881-0310 Jonathan K WattsRNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, MA 01605, USA.ORCID 0000-0001-5706-1734 The CRISPR Vision Program: Nonviral Genome Editing Platforms to Treat Inherited Retinal Channelopathies Epqt SupplementU19NS132296 · NINDS · UNIVERSITY OF WISCONSIN-MADISON · PI Krishanu Saha · 2023 to 2026
$36.8MPrecision Editing of Granulin Mutations that Cause Frontotemporal DementiaU01NS145218 · NINDS · UNIV OF MASSACHUSETTS MED SCH WORCESTER · PI GAO, FEN-BIAO, SONTHEIMER, ERIK J. · 2025 to 2025
$6.6MEnhancing CRISPR Gene Editing in Somatic Tissues by Chemical Modification of Guides and DonorsUH3TR002668 · NCATS · UNIV OF MASSACHUSETTS MED SCH WORCESTER · PI KHVOROVA, ANASTASIA, SONTHEIMER, ERIK J. · 2021 to 2022
$3.1MMid-Scale RNA Synthesis, Purification and Quality Control SystemS10OD020012 · OD · UNIV OF MASSACHUSETTS MED SCH WORCESTER · PI KHVOROVA, ANASTASIA · 2015 to 2015
$563k