Evidence mapPaperPMID 42479716Full record

SynthesisPloS one2026

Accuracy of the molecular diagnosis of duchenne and becker muscular dystrophy: A systematic review with meta-analysis.

Fabian A Chavez-Ecos, Carlos Quispe-Vicuña, Marco Malaga, Niels Pacheco-Barrios, Andrely Huerta-Rosario, Victor Velasquez-Rimachi, Peggy Martinez Esteban, Carlos Alva-Diaz

Abstract readSystematic ReviewMeta-Analysis
In one paragraph

Synthesis in PloS one, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

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field-weighted citation impact
1 · What the graph read from it

What it found

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The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

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3 · Its place in the literature

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4 · The record

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5 · Who and what money

Authors and funding

8 authors.

Fabian A Chavez-EcosGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.
Carlos Quispe-VicuñaGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.ORCID https://orcid.org/0000-0003-0076-0985
Marco MalagaGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.
Niels Pacheco-BarriosGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.
Andrely Huerta-RosarioGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.
Victor Velasquez-RimachiGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.
Peggy Martinez EstebanInstituto Nacional de Salud del Niño - San Borja, San Borja, Bolivia.
Carlos Alva-DiazGrupo de Investigación Neurociencias, Metabolismo, Efectividad Clínica y Sanitaria (NEMECS). Universidad Científica del Sur, Lima, Perú.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

introductionRecently, Molecular diagnosis of Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) has become increasingly important in the management of these patients, with techniques such as multiplex ligation-dependent amplification (MLPA) and next-generation sequencing (NGS) coming to the fore. Therefore, this study aims to evaluate the diagnostic accuracy of MLPA, NGS, and the algorithm MLPA-NGS for confirmatory diagnosis of DMD/BMD.

methodsWe systematically searched databases (PubMed, Embase, Scopus, Cochrane and Web of Science) until July 2025 for studies evaluating the diagnostic accuracy of MLPA and/or NGS testing in patients with clinical suspicion of DMD, considering multiplex PCR or biopsy as the reference test. A meta-analysis was performed using a random-effects model to estimate the sensitivity, specificity, and detection rate of each test. The QUADAS-2 tool was used to assess the risk of bias and the GRADE criteria were used to identify the certainty of evidence.

resultsWe included 10 studies (3786 patients) evaluating the use of MLPA and 14 studies (4333 patients) evaluating the use of NGS. For MLPA, the sensitivity was 0.80 (95%CI: 0.76-0.84; I2: 86%), the specificity was 0.93 (95%CI: 0.87-0.96; I2: 16%), and AUC 0.90 (CI-95%: 0.89-0.92). For NGS, the detection rate was 0.77 (95% CI: 0.61-0.87; I2: 94%). Furthermore, the detection rate increased to 0.97 (95% CI: 0.94-0.99; I2: 95%) when NGS was performed after MLPA. We observe a low risk of bias but with very low certainty in the estimations.

conclusionsIn patients with clinical suspicion of DMD, the MLPA test is very good but with very low certainty. However, in these patients with a negative MLPA, adding the NGS test would allow improve the detection rate. Therefore, the sequential use of these tests could be considered in patients who persist in the clinical suspicion.

Indexed as

Molecular Diagnostic TechniquesMuscular Dystrophy, DuchenneHigh-Throughput Nucleotide SequencingHumansMultiplex Polymerase Chain ReactionSensitivity and Specificity

Identifiers

PMID42479716
PMCPMC13387558

What Socratic holds

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.