Evidence map›Paper›PMID 42533192›Full record

ArticleCardiology and therapy2026

Rationale and Design of ACO-REAL: A Real-World Non-Interventional Study of Acoramidis in Routine Clinical Practice.

Marianna Fontana, Francesco Cappelli, Julian D Gillmore, Laura Obici, Fabian Aus dem Siepen, Philippe Debonnaire, Esther Gonzalez-Lopez, Marcel Schulze, Kai Vogtländer, Antonio Ciaccia and 2 more

2 registry-linked trialsAbstract read
PubMed Publisher
In one paragraph

Article in Cardiology and therapy, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. It is linked to 2 registered trials, which are not on this map. Not yet cited in PubMed.

0numbers the graph read from it
0cells of the map it votes in
0citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

NCT03860935 phase3completednot on this map

A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of the Efficacy and Safety of AG10 in Subjects With Symptomatic Transthyretin Amyloid Cardiomyopathy (ATTRibute-CM Trial)

TypeinterventionalSponsorEidos Therapeutics, a BridgeBio companyRan2019 to 2023Enrolled632ConditionsAmyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, CardiomyopathiesArmsacoramidis, Placebo Oral Tablet
NCT07235462 recruitingnot on this map

ACO-REAL - A Non-interventional Study Providing Insights Into the Use of Acoramidis in Patients With ATTR Amyloidosis With Cardiomyopathy (ATTR-CM) in Routine Clinical Practice

TypeobservationalSponsorBayerRan2025 to 2028Enrolled2,000ConditionsTransthyretin Amyloid Cardiomyopathy (ATTR-CM)ArmsAcoramidis (356 mg film-coated tablets)
3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

12 authors.

Marianna FontanaUniversity College London, London, UK. m.fontana@ucl.ac.uk.
Francesco CappelliTuscan Referral Center for Amyloid Treatment, Department of Clinical and Experimental Medicine, Careggi University Hospital, Florence, Italy.
Julian D GillmoreUniversity College London, London, UK.
Laura ObiciAmyloidosis Research and Treatment Centre, IRCCS Fondazione Policlinico San Matteo, Pavia, Italy.
Fabian Aus dem SiepenUniversity Hospital Heidelberg, Heidelberg, Germany.
Philippe DebonnaireSint-Jan Hospital Bruges, Brugge, Belgium.
Esther Gonzalez-LopezHospital Universitario Puerta de Hierro Majadahonda, IDIPHIM, CIBERCV, Madrid, Spain.
Marcel SchulzeBayer AG, Berlin, Germany.
Kai VogtländerMedical Affairs Statistics, Bayer AG, Wuppertal, Germany.
Antonio CiacciaBayer Inc, Global Medical and Evidence, Mississauga, ON, Canada.
Martin MerzBayer AG, Berlin, Germany.
Pablo Garcia-PaviaHospital Universitario Puerta de Hierro Majadahonda, IDIPHIM, CIBERCV, Madrid, Spain.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

introductionAcoramidis, an oral transthyretin stabilizer that achieves near-complete stabilization, is approved for the treatment of transthyretin amyloid cardiomyopathy (ATTR-CM) based on the phase 3 study, ATTRibute-CM (NCT03860935). To complement trial data, ACO-REAL (NCT07235462) was designed to generate real-world evidence on acoramidis use in ATTR-CM. This article describes the rationale and design of ACO-REAL.

methodsACO-REAL is an ongoing, prospective, non-interventional, multicenter study planned in approximately 2000 adults with ATTR-CM (wild-type or variant) initiating treatment with acoramidis in real-world settings across 21 European countries. The primary objective of ACO-REAL is to assess the characteristics and treatment patterns of participants with ATTR-CM receiving acoramidis during an observational period of around 12 months. PLANNED OUTCOMES: The primary objective is to assess demographics (including age and sex), disease characteristics, and treatment patterns of participants treated with acoramidis. Disease characteristics include type, diagnosis, and manifestations of ATTR-CM, and ATTR-CM-relevant comorbidities. Treatment patterns include adherence, persistence, and reasons for treatment modifications, including switching from a different ATTR-CM medication to acoramidis. The secondary objective is to describe the safety profile of acoramidis. The clinical course of ATTR-CM in participants initiating acoramidis is also being evaluated through measuring cardiac function, functional capacity and health status (New York Heart Association classification and 6-min walk distance), and health-related quality of life (Kansas City Cardiomyopathy Questionnaire and EuroQol 5-Dimension 5-Level questionnaire). Healthcare resource utilization is also being evaluated. Statistical analyses will be exploratory and descriptive. Categorical variables will be presented as frequencies and continuous variables as sample statistics.

conclusionsACO-REAL is the first multinational observational study to collect regular, prospective, real-world data in participants with ATTR-CM treated with acoramidis. This study aims to provide insights into ATTR-CM treatment using real-world evidence from European healthcare systems and may help to guide decision-making in clinical practice. Graphical abstract available for this article.

trial registrationClinicalTrials.gov identifier, NCT07235462.

Indexed as

AcoramidisReal-worldStudy designTransthyretin amyloid cardiomyopathyTreatment patterns

Identifiers

What Socratic holds

Textmetadata
Read underepoch 390

Registered trials

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the Socratic graph.